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Trial results

$RARE — DTX301 (avalotcagene ontaparvovec)

Ultragenyx Pharmaceutical Inc. (RARE) DTX301 (avalotcagene ontaparvovec): trial results in Ornithine transcarbamylase deficiency, 2027.

Research by Catalyst Intel

The catalyst

"Data are expected in the first half of 2027."

— Ultragenyx Pharmaceutical Inc., 8-K filed 2026-11-03 · the filing. Checked word for word against the stored document when this page was built; a sentence that did not check out would not be here.

Event id
RARE-DTX301AVALOT-2026
Company
Ultragenyx Pharmaceutical Inc.
Kind
Trial results
Indication
Ornithine transcarbamylase deficiency
Window
2027-01-01 – 2027-06-30
Status
dropped

The bar

No bar has been published for this event yet.

Verdicts

No verdict has been published for this event yet.